Sarepta's stock falls 48% after FDA critic Vinay Prasad's appointment and poor Elevidys sales. Company cuts revenue forecast ...

Attorneys general from 19 states and Washington, DC have filed a lawsuit against the federal government alleging that its ...

House and Senate lawmakers from both parties are working with the Trump administration on proposals that would use drug ...

The FDA on Tuesday said it is planning on doing more surprise inspections of foreign factories, a day after Trump signed an ...

The European Union is committing €500 million ($556 million) over the next two years to make Europe a “magnet” for ...

Vertex paused an early-stage trial of its inhaled treatment for cystic fibrosis that came from a partnership with Moderna.

Aldeyra Therapeutics reports Phase 3 success with reproxalap for dry eye disease, plans third FDA filing after previous ...

A Singapore-based startup raised a $45 million Series B to start testing a gene therapy in humans next year for a genetic ...

Vertex said it's gathering momentum with its new product launches, building out new franchises with its sickle cell therapy ...

Several members of an FDA advisory committee warned on Monday that new data from studies on long-term use of opioids might ...

PTC Therapeutics announced Monday that its splicing drug for Huntington’s disease met the primary endpoint of a Phase 2 study ...

Bristol Myers Squibb is letting go of 516 workers in New Jersey as part of a wide-reaching cost-cutting plan aimed at making ...