My son was lost to a rare disease 17 years ago. Now the outlook for patients is so much brighter

Rare diseases are not actually that rare. Collectively they affect 500 million people around the world. Some, such as Huntington’s disease and sickle cell disease, affect many thousands, others only ...
TheHealthSite

Rare Neurological Disorders: Subtle Early Brain Symptoms You Should Never Ignore

Unusual headaches, vision changes, mood shifts or numbness? Know the subtle early warning signs of rare neurological ...
TheHealthSite

Rare Disease Day 2026: Experts Reveal Why Certain Disorders Target Brain And Nervous System

Rare disease day is observed annually on the last day of February to spread awareness on certain conditions that can impact on patients lives.

GDC spoke with Children’s Hospital Colorado about Rare Disease Day

Today we want to touch upon rare disorders that impact not only adults but children as well!from rett syndrome, to ...
FierceBiotech

Servier Sharpens Its Focus on Rare Neurology

Rare neurology is entering a pivotal moment. Scientific understanding is accelerating, new technologies are maturing, and the patient need remains profoundly unmet. As the biopharmaceutical community ...
BioSpace

Rare Disease Groups Lobby for Regulatory Expediency as Makary Defends ‘Rigorous’ Approach

This week’s Capitol Hill meetings come on the heels of rejections of ultra-rare disease drugs developed by Biohaven and Saol Therapeutics. Physicians and patient groups implored the FDA to expedite ...

Living with a rare disease in India: What the healthcare system doesn’t see

Living with Isaacs' syndrome, a rare neurological condition, has made experience with healthcare challenging. Despite millions affected, support is limited.
WBTV on MSN

Rev. Jesse Jackson’s rare neurological disorder often misdiagnosed, doctor says

Jackson was diagnosed with Parkinson’s disease in 2015.