The efficacy of gene therapy for treating the heart disease associated with Friedreich's ataxia, a rare hereditary neuro-degenerative disorder, has been demonstrated in a mouse model. Friedreich's ...

Friedreich’s ataxia is a rare genetic disease that causes difficulty walking, a loss of sensation in the arms and legs, and impaired speech. It’s also known as spinocerebellar degeneration. “Ataxia” ...

Difficulty balancing or an inability to do so can be caused by any number of factors. Head injuries, migraines, alcohol use, ear infections and medications can all affect your musculoskeletal system ...

If you have impaired muscle coordination or control, you might have a type of ataxia. This condition is rare, but it can make it difficult to maintain balance, speak, or move. “Ataxia” is the medical ...

Ataxia is a lack of muscle coordination that may affect a person’s speech, eye movements, and ability to swallow, walk, and pick up objects. It can happen due to certain health conditions, genetics, ...

Ataxia is a form of movement disorder. There is loss of balance and physical co-ordination leading to difficulty in walking normally. The Cerebellum of the brain is normally responsible for ...

The transfer, via a viral vector, of a normal copy of the gene deficient in patients, allowed to fully and very rapidly cure the heart disease in mice. These findings are published in Nature Medicine ...